Who may participate

Each clinical study has its own guidelines for who may participate, called eligibility criteria. These factors can include your age, sex, overall health, type and stage of disease, and personal treatment history. However, only the research study staff can determine if you qualify to enroll in the study.

Condition

Spinal Muscular Atrophy, Neuromuscular Diseases, SMA

Sex

Male or Female

Age

4 - 21 years

View more eligibility criteria on ClinicalTrials.gov
Study Locations

Phoenix Children's

Phoenix, Arizona, United States, 85016
Recruiting
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UCSD & Rady Children's

La Jolla, California, United States, 92037
Recruiting
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Children's Hospital of Los Angeles

Los Angeles, California, United States, 90027
Recruiting
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UCSF Benioff Children's Hospital, Medical Center

San Francisco, California, United States, 94158
Recruiting
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Children's Hospital Colorado

Aurora, Colorado, United States, 80045
Recruiting
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UF Health, Shands Hospital

Gainesville, Florida, United States, 32610
Recruiting
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Rare Disease Research

Atlanta, Georgia, United States, 30329
Recruiting
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Northwestern University - Feinberg School of Medicine - Ann & Robert H. Lurie Children's Hospital of Chicago

Chicago, Illinois, United States, 60611
Recruiting
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Indiana University -Riley Research

Indianapolis, Indiana, United States, 46202
Recruiting
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University of Iowa

Iowa City, Iowa, United States, 52242
Recruiting
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University of Kansas Medical Center

Fairway, Kansas, United States, 66205
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Boston Children's Hospital - Harvard

Boston, Massachusetts, United States, 02115
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BSHS Office of Research

Grand Rapids, Michigan, United States, 49503
Recruiting
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Washington University in St. Louis

Saint Louis, Missouri, United States, 63110
Recruiting
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Columbia University Medical Center

New York, New York, United States, 10032
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Stony Brook University Hospital

Stony Brook, New York, United States, 11794
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Duke University Medicine

Durham, North Carolina, United States, 27705
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Cincinnati Children's Hospital Medical Center

Cincinnati, Ohio, United States, 45229
Recruiting
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Nationwide Children's Hospital

Columbus, Ohio, United States, 43205
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Penn State College of Medicine

Hershey, Pennsylvania, United States, 17033
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CHOP Children's Hospital of Philadelphia

Philadelphia, Pennsylvania, United States, 19104
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UPMC Children's Hospital of Pittsburgh

Pittsburgh, Pennsylvania, United States, 15224
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Vanderbilt University Medical Center

Nashville, Tennessee, United States, 37232
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UT Pediatric Neurosciences/Dell Children's Medical Center

Austin, Texas, United States, 78723
Recruiting
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Neurology Rare Disease Center

Denton, Texas, United States, 75208
Recruiting
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Cook Children's Hospital

Fort Worth, Texas, United States, 76104
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University of Virginia Children's Hospital

Charlottesville, Virginia, United States, 22903
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Children's Hospital of The King's Daughters

Norfolk, Virginia, United States, 23507
Recruiting
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MultiCare Institute of Research and Innovation

Tacoma, Washington, United States, 98405
Recruiting
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Medical College of Wisconsin

Milwaukee, Wisconsin, United States, 53226
Recruiting
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University Hospital Antwerp

Edegem, Belgium, 02650
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University Hospital Ghent

Ghent, Belgium, 09000
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University Hospital Leuven

Leuven, Belgium, 03000
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University Hospital Brno - Dept. of Pediatric Neurology

Brno, Czechia, 625 00
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Motol University Hospital

Prague, Czechia, 150 06
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University Hospital Essen (Public-Law Institution) - Dept. of Pediatrics I

Essen, Germany, 45147
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University Hospital Freiburg, Center For Children and Adolescent Medicine, Dept. of Neuropediatrics and Muscle Disorders

Freiburg, Germany, 79106
Recruiting
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Dr. Von Haunersches Children'S Hospital - Lmu Munich

Munich, Germany, 80337
Recruiting
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Irccs Institute of Neurological Sciences of Bologna - Bellaria Hospital

Bologna, Italy, 40139
Recruiting
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Nemo-Brescia Clinical Center For Neuromuscular Diseases

Gussago, Italy, 25064
Recruiting
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IRCCS NEUROLOGICAL INSTITUTE C. MONDINO CHILD and NEUROPSYCHIATRIC UNIT

Pavia, Italy, 27100
Recruiting
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Bambino Gesù Children'S Research Hospital Irccs - San Paolo Office Dept. of Neuroscience

Roma, Italy, 00165
Recruiting
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University Medical Center Utrecht

Utrecht, Netherlands, 3584 CX
Recruiting
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University Clinical Centre in Gdansk - Dept. of Developmental Neurology

Gdańsk, Poland, 80-925
Recruiting
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Heliodor Swiecicki Clinical Hospital At Medical University - Child and Adolescents Neurology Clinic

Poznań, Poland, 60-355
Recruiting
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The Children'S Memorial Health Institute - Dept. of Neurology and Epileptology

Warsaw, Poland, 04-730
Recruiting
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T. Marciniak Lower Silesian Specialist Hospital, Pediatric Neurology Dept.

Wrocław, Poland, 54-049
Recruiting
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Donostia University Hospital

Donostia, Spain, 20014
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Hospital Sant Joan de Déu

Esplugues De Llobregat, Spain, 08950
Recruiting
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Maternal-Child'S Hospital of Málaga, Regional University Hospital - Pediatric Neurology Unit

Málaga, Spain, 29011
Recruiting
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La Fe University and Polytechnic Hospital

Valencia, Spain, 46026
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Royal Hospital For Children

Glasgow, Scotland, United Kingdom, G51 4TF
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John Radcliffe Hospital

Oxford, United Kingdom, OX3 9DU
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Yale University

New Haven, Connecticut, United States, 06511
Not yet recruiting
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Children's National Medical Center

Washington, District of Columbia, United States, 20010
Not yet recruiting
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Baylor College of Medicine at The Children's Hospital of San Antonio

San Antonio, Texas, United States, 89207
Not yet recruiting
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Chr Citadella

Liège, Belgium, 04000
Not yet recruiting
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Royal Manchester Children'S Hospital

Manchester, United Kingdom, M13 9WL
Not yet recruiting
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