NCT05337553

Spinal Muscular Atrophy

Who may participate

Each clinical study has its own guidelines for who may participate, called eligibility criteria. These factors can include your age, sex, overall health, type and stage of disease, and personal treatment history. However, only the research study staff can determine if you qualify to enroll in the study.

Condition

Spinal Muscular Atrophy, Neuromuscular Diseases, SMA

The disease, disorder, syndrome, illness, or injury that is being studied. On ClinicalTrials.gov, conditions may also include other health-related issues, such as lifespan, quality of life, and health risks.
Sex
Male or Female
The sex of people who may participate in a clinical trial (all, female, male). Sex is a person’s classification based on assignment at birth. Eligibility based on sex is distinct from eligibility based on gender.
Age
4 - 21 years
The age a person must be to participate in a clinical trial.
View more eligibility criteria on ClinicalTrials.gov

Study Locations

Study Locations
59 trials found.

UCSD & Rady Children's

La Jolla, California, United States, 92037
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Children's Hospital of Los Angeles

Los Angeles, California, United States, 90027
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Children's Hospital Colorado

Aurora, Colorado, United States, 80045
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UF Health, Shands Hospital

Gainesville, Florida, United States, 32610
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Rare Disease Research

Atlanta, Georgia, United States, 30329
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Northwestern University - Feinberg School of Medicine - Ann & Robert H. Lurie Children's Hospital of Chicago

Chicago, Illinois, United States, 60611
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Indiana University -Riley Research

Indianapolis, Indiana, United States, 46202
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University of Iowa

Iowa City, Iowa, United States, 52242
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University of Kansas Medical Center

Fairway, Kansas, United States, 66205
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Boston Children's Hospital - Harvard

Boston, Massachusetts, United States, 02115
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BSHS Office of Research

Grand Rapids, Michigan, United States, 49503
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Washington University in St. Louis

Saint Louis, Missouri, United States, 63110
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Columbia University Medical Center

New York, New York, United States, 10032
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Stony Brook University Hospital

Stony Brook, New York, United States, 11794
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Duke University Medicine

Durham, North Carolina, United States, 27705
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Cincinnati Children's Hospital Medical Center

Cincinnati, Ohio, United States, 45229
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Nationwide Children's Hospital

Columbus, Ohio, United States, 43205
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Penn State College of Medicine

Hershey, Pennsylvania, United States, 17033
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UPMC Children's Hospital of Pittsburgh

Pittsburgh, Pennsylvania, United States, 15224
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Vanderbilt University Medical Center

Nashville, Tennessee, United States, 37232
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Neurology Rare Disease Center

Denton, Texas, United States, 75208
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Cook Children's Hospital

Fort Worth, Texas, United States, 76104
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University of Virginia Children's Hospital

Charlottesville, Virginia, United States, 22903
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MultiCare Institute of Research and Innovation

Tacoma, Washington, United States, 98405
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Medical College of Wisconsin

Milwaukee, Wisconsin, United States, 53226
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University Hospital Ghent

Ghent, Belgium, 09000
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University Hospital Leuven

Leuven, Belgium, 03000
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Irccs Institute of Neurological Sciences of Bologna - Bellaria Hospital

Bologna, Italy, 40139
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University Medical Center Utrecht

Utrecht, Netherlands, 3584 CX
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The Children'S Memorial Health Institute - Dept. of Neurology and Epileptology

Warsaw, Poland, 04-730
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Hospital Sant Joan de Déu

Esplugues De Llobregat, Spain, 08950
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La Fe University and Polytechnic Hospital

Valencia, Spain, 46026
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Phoenix Children's

Phoenix, Arizona, United States, 85016
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UCSF Benioff Children's Hospital, Medical Center

San Francisco, California, United States, 94158
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Yale University

New Haven, Connecticut, United States, 06511
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Children's National Medical Center

Washington, District of Columbia, United States, 20010
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Johns Hopkins

Baltimore, Maryland, United States, 21287
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CHOP Children's Hospital of Philadelphia

Philadelphia, Pennsylvania, United States, 19104
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UT Pediatric Neurosciences/Dell Children's Medical Center

Austin, Texas, United States, 78723
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Baylor College of Medicine at The Children's Hospital of San Antonio

San Antonio, Texas, United States, 89207
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Children's Hospital of The King's Daughters

Norfolk, Virginia, United States, 23507
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University Hospital Antwerp

Edegem, Belgium, 02650
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Chr Citadella

Liège, Belgium, 04000
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University Hospital Brno - Dept. of Pediatric Neurology

Brno, Czechia, 625 00
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Motol University Hospital

Prague, Czechia, 150 06
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University Hospital Essen (Public-Law Institution) - Dept. of Pediatrics I

Essen, Germany, 45147
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University Hospital Freiburg, Center For Children and Adolescent Medicine, Dept. of Neuropediatrics

Freiburg, Germany, 79106
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Dr. Von Haunersches Children'S Hospital - Lmu Munich

Munich, Germany, 80337
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Nemo-Brescia Clinical Center For Neuromuscular Diseases

Gussago, Italy, 25064
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Irccs Neurological Institute C. Mondino - Child Neuropsychiatric Unit

Pavia, Italy, 27100
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Bambino Gesù Children'S Research Hospital Irccs - San Paolo Office Dept. of Neuroscience

Roma, Italy, 00165
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University Clinical Centre in Gdansk - Dept. of Developmental Neurology

Gdańsk, Poland, 80-925
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Heliodor Swiecicki Clinical Hospital At Medical University - Child and Adolescents Neurology Clinic

Poznań, Poland, 60-355
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T. Marciniak Lower Silesian Specialist Hospital, Pediatric Neurology Dept.

Wrocław, Poland, 54-049
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Donostia University Hospital

Donostia, Spain, 20014
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Maternal-Child'S Hospital of Málaga, Regional University Hospital - Pediatric Neurology Unit

Málaga, Spain, 29011
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Royal Hospital For Children

Glasgow, Scotland, United Kingdom, G51 4TF
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Royal Manchester Children'S Hospital

Manchester, United Kingdom, M13 9WL
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John Radcliffe Hospital

Oxford, United Kingdom, OX3 9DU
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